Gene Therapy in Dubai – Advanced Treatment for Genetic Disorders

Gene Therapy in Dubai – Advanced Treatment for Genetic Disorders

Gene therapy is a revolutionary approach in modern medicine that aims to treat or prevent diseases by modifying a person’s genes. This cutting-edge treatment is especially promising for genetic disorders like spinal muscular atrophy (SMA) and Duchenne muscular dystrophy (DMD), offering hope for patients and families affected by these life-limiting conditions. Our center in Dubai is committed to delivering safe and effective gene therapy options tailored to each patient’s needs.

What is Gene Therapy?

Gene therapy in Dubai involves introducing, removing, or altering genetic material within a patient’s cells to correct faulty genes or make beneficial changes. The goal is to address the root cause of genetic disorders rather than just manage the symptoms. There are several types of gene therapy approaches, including...

Gene replacement therapy

Replacing a missing or faulty gene with a healthy copy.

Gene editing

Precisely correcting mutations at the DNA level using technologies like CRISPR.

Gene silencing

Switching off the expression of a harmful gene.

Gene therapy is administered using viral or non-viral vectors that deliver the therapeutic gene into the body, often via a one-time infusion.

Conditions Treated with Gene Therapy

Gene therapy has shown remarkable success in treating various inherited disorders, including

Spinal Muscular Atrophy (SMA)

Treatments like Zolgensma provide a functional copy of the SMN1 gene to restore motor neuron function.

Duchenne Muscular Dystrophy (DMD)

Ongoing research and trials are developing gene therapies that enable the body to produce functional dystrophin protein.

Inherited retinal diseases, thalassemia, sickle cell disease,

and other rare conditions are also being targeted by gene therapy solutions.

Benefits and Considerations

Potential one-time treatment for lifelong results

Targets the root cause of the disease

Reduces or eliminates the need for ongoing medications or surgeries

Improves quality of life and long-term outcomes

Considerations and limitations

Not all genetic disorders currently have approved gene therapies

High cost and need for specialized infrastructure

Potential immune responses or side effects

Long-term effects still being studied in ongoing clinical trials

We ensure a thorough evaluation and counseling process for every patient to determine eligibility and discuss risks, benefits, and expectations

Gene Therapy Process and Treatment at Our Dubai Center

At our state-of-the-art medical facility in Dubai, we offer a streamlined and safe approach to gene therapy:

Genetic testing and diagnosis to confirm eligibility

Pre-treatment evaluations including cardiac, respiratory, and immune assessments

Gene therapy administration under the care of a multidisciplinary team

Post-treatment monitoring for side effects and effectiveness

Family support and counseling throughout the treatment journey

We are proud to be among the few specialized centers in the region offering access to advanced gene therapy treatments for children and families impacted by serious genetic conditions, led by Dr. Vivek Mundada, a renowned pediatric neurologist in Dubai.